KIT-20, a promising therapy for Leigh Syndrome, has been granted Orphan Drug and Rare Pediatric Drug Designations by the US FDA. This marks another milestone achievement for NeuroCores in our journey to develop treatments for rare pediatric neurological disorders.
There are now 2 pipeline assets – KIT-13 for Rett Syndrome and KIT-20 for Leigh Syndrome – that have been granted both Orphan Drug and Rare Pediatric Drug Designations by the US FDA.